Rett Syndrome Research Trust

Rare diseases don?t cure themselves. Developing genetic medicines is a complex, expensive effort with many moving parts. We are the organization orchestrating this global effort, and here is our plan to cure Rett syndrome.

As the largest worldwide funder of Rett research, we're advancing genetic medicines that target the root cause of Rett. The gene therapy programs currently in clinical trials were started and incubated at RSRT. We are the go-to partner for genetic medicine scientists and companies.

The commitment and passion of Rett families in the US and around the globe make our critical work possible. If you want a cure as urgently as we do, we welcome you to our site and invite you to join us in our quest.